Rylea-Ann was unable to walk before receiving the gene therapy Judy Wei
A gene-replacement therapy that is administered directly to the brain has allowed some children with a rare genetic condition to walk and talk for the first time.
鈥淚t鈥檚 a dream come true,鈥 says Richard Poulin, whose daughter Rylae-Ann received the therapy in November 2019, aged 18 months. Rylae-Ann, who lives in Thailand, went from being unable to say any words, move or even lift her head to 鈥渞unning, jumping, kicking a ball, riding a horse, swimming and speaking in multiple languages鈥, according to Poulin.
Rylae-Ann was born…
